Simple Science

Cutting edge science explained simply

Cutting edge science explained simply

L. Newton

Genetic and Genomic Medicine Advancements in Antisense Oligonucleotide Therapies for Rare Diseases

New guidelines and treatments offer hope for rare disease patients.

Marlen Lauffer, D. Cheerie, M. Meserve

2025-06-09T12:07:30+00:00 ― 6 min read